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EMA Product

Skytrofa (previously Lonapegsomatropin Ascendis Pharma)

Product approved by European Medicines Agency (EU)

Basic Information

Skytrofa (previously Lonapegsomatropin Ascendis Pharma)

Regulatory Information

EMEA/H/C/005367

Authorised

January 11, 2022

November 11, 2021

5

February 12, 2025

Company Information

Denmark

Tuborg Boulevard 12 2900 Hellerup

Ascendis Pharma Endocrinology Division A/S

Drug Classification

Orphan MedicineAdditional Monitoring

Active Substances Detail

Detailed Information

Therapeutic Indication

### Therapeutic indication Growth failure in children and adolescents aged from 3 years up to 18 years due to insufficient endogenous growth hormone secretion (growth hormone deficiency \[GHD\])

Overview Summary

Lonapegsomatropin Ascendis Pharma is a medicine that is used to improve growth in children and adolescents who do not produce enough growth hormone (growth hormone deficiency or GHD). The medicine is intended for children and adolescents from 3 up to 18 years of age. GHD is rare, and Lonapegsomatropin Ascendis Pharma was designated an ‘orphan medicine’ (a medicine used in rare diseases) on 17 October 2019. Further information on the orphan designation can be found here: [ema.europa.eu/medicines/human/orphan-designations/eu3192213](/en/medicines/human/orphan-designations/eu-3-19-2213). Lonapegsomatropin Ascendis Pharma contains the active substance lonapegsomatropin.

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