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Ionis Pharmaceuticals

🇺🇸United States
Ownership
-
Employees
927
Market Cap
$7B
Website
Introduction

Ionis Pharmaceuticals, Inc. engages in the development and commercialization of human therapeutic drugs using antisense technology. It operates through the Ionis Core segment. The Ionis Core segment exploits a novel drug discovery platform to generate a pipeline of drugs. The company was founded by Stanley T. Crooke, David J. Ecker, Christopher K. Mirabelli, and Brett P. Monia on January 10, 1989 and is headquartered in Carlsbad, CA.

Clinical Trials

4

Active:3
Completed:0

Trial Phases

2 Phases

Phase 1:3
Phase 3:1

Drug Approvals

0

Drug Approvals

No drug approvals found

This company may not have drug approvals in our database

Clinical Trials

Distribution across different clinical trial phases (4 trials with phase data)• Click on a phase to view related trials

Phase 1
3 (75.0%)
Phase 3
1 (25.0%)
No trials found

News

Sarepta Therapeutics Implements $400 Million Cost-Cutting Plan Amid Regulatory Challenges for Gene Therapy

Sarepta Therapeutics announced a $400 million annual cost-savings initiative in July 2025, including a 36% workforce reduction of 500 employees to achieve financial sustainability through 2027.

Biogen Advances Salanersen to Phase 3 Studies for Spinal Muscular Atrophy After Promising Results

Biogen's salanersen (BIIB115/ION306) demonstrated substantial slowing of neurodegeneration and clinically meaningful motor function improvements in children with spinal muscular atrophy previously treated with gene therapy.

CNS Oligonucleotide Licensing Deals Surge 339% to $2.81 Billion in 2024

Licensing agreements for CNS-targeted oligonucleotide therapeutics increased 339% from 2023 to 2024, reaching $2.81 billion in total deal value according to GlobalData's analysis.

Ulefnersen Shows Unprecedented Recovery in Young Patients with Rare FUS-ALS

Columbia University researchers report that ulefnersen, an experimental drug, demonstrated remarkable efficacy in treating FUS-ALS, a rare genetic form of ALS affecting young people.

Ionis Reports Positive Phase 3 Results for Olezarsen in Hypertriglyceridemia

Olezarsen demonstrated significant triglyceride reductions of 61% and 58% at 6 months with 80mg and 50mg monthly doses respectively in patients with moderate hypertriglyceridemia.

Ionis and Ono Forge $940 Million Deal for Sapablursen in Polycythemia Vera Treatment

Ionis Pharmaceuticals has licensed sapablursen, an RNA-targeted medicine for polycythemia vera, to Ono Pharmaceutical in a deal worth up to $940 million including $280 million upfront.

EU Approves WAINZUA (Eplontersen) for Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

The European Commission has approved WAINZUA (eplontersen), developed by Ionis Pharmaceuticals and AstraZeneca, for treating hereditary transthyretin-mediated amyloidosis with polyneuropathy (ATTRv-PN) in adult patients with stage 1 or 2 disease.

Ionis Advances Antisense Therapy for Angelman Syndrome to Phase 3 Following Promising Clinical Results

Ionis Pharmaceuticals is moving forward with Phase 3 trials for ION582, an antisense therapy designed to unsilence the paternal UBE3A gene in Angelman syndrome patients, after Biogen declined to license the drug.

Major Advances in Angioedema Pipeline: Intellia's Gene Therapy Enters Phase 3 as Multiple Companies Race for Novel Treatments

Intellia Therapeutics has initiated Phase 3 trials for NTLA-2002, a groundbreaking CRISPR-based gene therapy for hereditary angioedema, with potential U.S. launch targeted for 2027.

Novartis Pushes Back Phase 3 Data Timeline for Ionis-Partnered Cardiac Therapy

• Novartis announced during its Q4 2024 financial results that the timeline for Phase 3 trial data of its cardiac therapy, developed in partnership with Ionis Pharmaceuticals, will be delayed. • The strategic collaboration between Novartis and Ionis Pharmaceuticals faces a setback in their cardiovascular drug development program, impacting their clinical trial readout schedule.

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