RETT SYNDROME RESEARCH TRUST
🇺🇸United States
- Country
- 🇺🇸United States
- Ownership
- -
- Established
- 2008-01-01
- Employees
- -
- Market Cap
- -
- Website
- https://reverserett.org/
Apertura Gene Therapy Partners with Rett Syndrome Research Trust to Advance Blood-Brain Barrier-Crossing Gene Therapy Platform
Apertura Gene Therapy and Rett Syndrome Research Trust announced a collaboration to license Apertura's TfR1-targeted AAV capsid technology for developing genetic medicines to treat Rett syndrome.
ProQR Advances RNA Editing Pipeline with Four Clinical Readouts Expected by 2026
ProQR Therapeutics is advancing its Axiomerâ„¢ RNA editing platform across liver and CNS programs, with its lead program AX-0810 for cholestatic diseases on track for CTA filing in Q2 2025.
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