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Praxis Precision Medicines

Praxis Precision Medicines logo
🇺🇸United States
Ownership
Public
Established
2015-09-22
Employees
82
Market Cap
$950.3M
Website
http://www.praxismedicines.com
Introduction

Praxis Precision Medicines, Inc. is a clinical-stage biopharmaceutical company, which engages in the genetic epilepsies into the development of therapies for central nervous system, or CNS, disorders characterized by neuronal excitation-inhibition imbalance. It focuses on two proprietary platforms: Cerebrum and Solidus. The Cerebrum platform utilizes a deep understanding of neuronal excitability and neuronal networks and applies a series of computational and experimental tools to develop orally available precision therapies. The Solidus platform consists of antisense oligonucleotide, or ASO. It is a targeted precision medicine discovery and development engine anchored on a proprietary, computational methodology. The company was founded by Kiran Reddy, David Goldstein, and Steven Petrou on September 22, 2015 and is headquartered in Boston, MA.

statnews.com
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Eli Lilly seeks to join lawsuit on compounded drugs

STAT's biotech newsletter highlights key sector events, including Ultragenyx and Praxis's Phase 3 trials, Trump's FDA transition plan, Eli Lilly's lawsuit involvement over tirzepatide, and Biden's science and tech awards to CRISPR scientists and mRNA vaccine developers.
stocktitan.net
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Praxis Precision Medicines to Present at J.P. Morgan Healthcare Conference

Praxis Precision Medicines (NASDAQ: PRAX) will present at the 43rd Annual J.P. Morgan Healthcare Conference on January 15, 2025, in San Francisco. The presentation, focusing on CNS disorder therapies, will be webcast live and available for replay on the company's website for 30 days.
statnews.com
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The biotech scorecard for the first quarter: 16 stock-moving events to watch

Ultragenyx is developing setrusumab for Osteogenesis Imperfecta, with Phase 3 study results expected soon. Praxis Precision Medicines is working on ulixacaltamide for essential tremor, also awaiting Phase 3 study results this quarter.
au.investing.com
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UNITY Biotech appoints new chief medical officer

UNITY Biotechnology appoints Federico Grossi, M.D., Ph.D., as chief medical officer to advance its age-related disease treatments. Grossi's expertise in clinical development and regulatory strategy, especially in ophthalmology, is expected to boost UNITY's therapeutic portfolio, including the Phase 2b ASPIRE study of UBX1325 for diabetic macular edema.
nasdaq.com
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FDA Grants Rare Pediatric Disease Designation To Praxis' Relutrigine For Dravet Syndrome

Praxis Precision Medicines received FDA's Rare Pediatric Disease Designation for Relutrigine, targeting Dravet syndrome, a severe genetic epilepsy. Relutrigine inhibits persistent sodium current, addressing seizure symptoms. The drug also has Orphan Drug Designations for SCN2A and SCN8A DEEs, with ongoing Phase 2 study results expected by 2026.
marketscreener.com
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Praxis Precision Medicines, Inc. Announces Rare Pediatric Disease Designation Granted for relutrigine

Praxis Precision Medicines' relutrigine received FDA's Rare Pediatric Disease Designation for Dravet syndrome. EMBOLD study results showed 46% placebo-adjusted monthly motor seizure reduction, over 30% seizure freedom, and 77% median seizure rate reduction. Praxis is enrolling for a second cohort, expecting topline results in H1 2026.
globenewswire.com
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Praxis Precision Medicines Announces Rare Pediatric Disease

Praxis Precision Medicines receives Rare Pediatric Disease Designation for relutrigine in Dravet syndrome, reflecting commitment to addressing unmet needs in rare neurological disorders. Praxis plans to initiate an all-DEE trial (EMERALD) in 1H2025.
finance.yahoo.com
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Praxis Precision Medicines Announces Rare Pediatric Disease Designation Granted for relutrigine in Dravet syndrome

Praxis Precision Medicines received FDA's Rare Pediatric Disease Designation for relutrigine in Dravet syndrome. Relutrigine, a first-in-class small molecule, aims to treat developmental and epileptic encephalopathy, with encouraging clinical data showing reduced seizure frequency and improved control. Praxis plans to initiate an all-DEE trial (EMERALD) in 1H2025.
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