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Gene therapy, a medical technique modifying genes to treat diseases, is growing rapidly. The US market, valued at $1,312.2M in 2024, is expected to reach $3,697.8M by 2033. Key growth drivers include genetic disorder prevalence, advancements in genetic engineering, and R&D investments. The article lists 10 top gene therapy stocks to buy, highlighting their potential in treating diseases like sickle cell disease and Alzheimer's.

Gene therapy, a transformative medical approach, is gaining momentum for treating diseases by altering genetic material. With advancements and investments, the market is expected to exceed USD 10 billion by 2025, despite challenges like high costs and regulatory hurdles.

The 'Beta Thalassaemia - Global Clinical Trials Review, 2024' report by ResearchAndMarkets.com offers an overview of clinical trials, including trial numbers, enrollment, regions, countries, phases, status, and sponsor types. It highlights prominent drugs and companies involved, aiding decision-making and identifying opportunities in the global clinical trials market.

Deshawn “DJ” Chow, a 19-year-old with sickle cell disease, received Casgevy, a groundbreaking gene-editing treatment using Crispr technology, at City of Hope. This one-time therapy, involving stem cell collection and editing, offers a potential end to pain crises. Despite its approval, the treatment's rollout is slow due to manufacturing and insurance challenges.

CRISPR Therapeutics' stock has declined despite regulatory approvals for Casgevy, a gene-editing treatment for sickle cell disease and beta-thalassemia. Despite its high cost, a U.S. government plan aims to improve Medicaid patients' access. With a potential market of 58,000 patients and peak sales possibly exceeding $2.2 billion, CRISPR's future includes expanding its gene-editing treatments beyond Casgevy.

2024 saw breakthroughs in gene therapies for sickle cell disease, at-home flu vaccines, mind-controlled prosthetics, non-opioid pain medicine, AI medical scribes, fruit fly brain mapping, clinical-grade hearing aids, new schizophrenia drugs, brain-computer interfaces, HIV prevention meds, cervical cancer screening alternatives, maternal health apps, AI protein structure prediction, VR for mental health, screen time reduction tools, gene therapy for deafness, women's health research, self-serve vision tests, blood tests for colorectal cancer, and potential lupus cures.

The CAR-T cell therapy market, valued at USD 7.31 billion in 2024, is expected to grow at a CAGR of 36.8% to USD 188.84 billion by 2034. This growth is driven by R&D advancements and the therapy's effectiveness against cancers like lymphoma and leukemia, even when other treatments fail.

The CAR-T cell therapy market, valued at USD 7.31 billion in 2024, is expected to grow to USD 188.84 billion by 2034, with a CAGR of 36.8%. This growth is driven by advancements in cancer treatment, particularly for lymphoma, leukemia, and multiple myeloma, and the rising prevalence of cancers like DLBCL. North America leads the market due to advanced healthcare infrastructure and significant R&D investments.