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Translate Bio, Inc.

Translate Bio, Inc. logo
🇺🇸United States
Ownership
Public, Subsidiary
Established
2011-01-01
Employees
122
Market Cap
-
Website
http://translate.bio

Safety, Tolerability and PK/PD Evaluation of Intravenous Administration of MRT5201 in Patients With OTC Deficiency

Phase 1
Withdrawn
Conditions
Ornithine Transcarbamylase Deficiency
Interventions
Biological: MRT5201
Other: Placebo
First Posted Date
2018-12-06
Last Posted Date
2019-09-17
Lead Sponsor
Translate Bio, Inc.
Registration Number
NCT03767270

Study to Evaluate the Safety & Tolerability of MRT5005 Administered by Nebulization in Adults With Cystic Fibrosis

Phase 1
Conditions
Cystic Fibrosis
Interventions
Drug: Normal saline
First Posted Date
2017-12-15
Last Posted Date
2020-11-16
Lead Sponsor
Translate Bio, Inc.
Target Recruit Count
40
Registration Number
NCT03375047
Locations
🇺🇸

Johns Hopkins University, Baltimore, Maryland, United States

🇺🇸

University of Alabama at Birmingham, Birmingham, Alabama, United States

🇺🇸

National Jewish Health, Denver, Colorado, United States

and more 15 locations
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