Marinus Pharmaceuticals, Inc. is a biopharmaceutical company, which engages in the development and commercialization of neuropsychiatric therapeutics. Its clinical stage drug product candidate, ganaxolone, is a positive allosteric modulator being developed in three different dose forms: intravenous, capsule, and liquid. The company was founded in August 2003 and is headquartered in Radnor, PA.
Swedish rare disease specialist Immedica Pharma has agreed to acquire Marinus Pharmaceuticals for $151M, strengthening its position in the global rare disease market through a cash tender offer of $0.55 per share.
Marinus Pharmaceuticals announced a workforce reduction of approximately 45% following disappointing Phase III trial results for oral ganaxolone in tuberous sclerosis complex.
Marinus Pharmaceuticals shifts focus to oral ganaxolone (O-GNX) for tuberous sclerosis complex (TSC) after IV ganaxolone (IV-GNX) fails a Phase 3 trial for refractory status epilepticus (RSE).
Amgen has launched Pavblu, its biosimilar to Regeneron's Eylea, at a 10% discount, pricing it at $1,665 per dose, potentially muting its market impact.
Marinus Pharmaceuticals' Phase III TrustTSC trial of oral ganaxolone for tuberous sclerosis complex (TSC)-associated seizures did not meet its primary endpoint.
Marinus Pharmaceuticals' Phase 3 TrustTSC trial evaluating oral ganaxolone for tuberous sclerosis complex (TSC)-associated seizures did not meet its primary endpoint.
Marinus Pharmaceuticals' Phase 3 TrustTSC trial of oral ganaxolone for tuberous sclerosis complex (TSC)-associated seizures did not meet its primary endpoint.
Marinus Pharmaceuticals' RAISE trial evaluated IV ganaxolone for refractory status epilepticus (RSE), meeting one co-primary endpoint.
Marinus Pharmaceuticals anticipates Phase 3 TrustTSC trial results for ZTALMY® in tuberous sclerosis complex (TSC) in Q4 2024, with NDA filing targeted for April 2025.