Ultragenyx Pharmaceutical
- Country
- 🇨🇱Chile
- Ownership
- -
- Employees
- 1.2K
- Market Cap
- -
- Introduction
Tactical Resources Corp is an exploration & development company focused on the rare earth elements (REE) that drive the green technologies of the future. Its projects include Lac Ducharme Project, Peak Project, and SAM Gold Project.
Evkeeza Approved in EU for HoFH Treatment in Children as Young as 6 Months
The European Commission has approved Evkeeza (evinacumab) for treating children aged six months and older with homozygous familial hypercholesterolemia (HoFH).
Setrusumab Receives FDA Breakthrough Therapy Designation for Osteogenesis Imperfecta
The FDA granted Breakthrough Therapy Designation to setrusumab for reducing fracture risk in osteogenesis imperfecta (OI) types I, III, and IV, for patients aged 2 years and older.
Ultragenyx's GTX-102 Shows Sustained Improvement in Angelman Syndrome Patients in Phase 1/2 Data
Ultragenyx's GTX-102, an investigational antisense oligonucleotide, demonstrates continued improvement across multiple domains in Angelman syndrome patients at Week 48 in Phase 1/2 data.
Ultragenyx's GTX-102 Shows Promise in Angelman Syndrome Phase 1/2 Trial
Ultragenyx presented positive Phase 1/2 data for GTX-102, an antisense oligonucleotide targeting Angelman syndrome, at the FAST Global Science Summit.