Biomarin Pharmaceutical
- Country
- 🇨🇦Canada
- Ownership
- -
- Established
- 1997-01-01
- Employees
- -
- Market Cap
- $17.2B
- Website
- http://www.biomarin.com
Extension Study for Patients Who Have Participated in a BMN 701 Study
- First Posted Date
- 2011-09-19
- Last Posted Date
- 2018-05-22
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 21
- Registration Number
- NCT01435772
- Locations
- 🇺🇸
Univ of California San Diego School of Medicine, San Diego, California, United States
🇺🇸University of Florida College of Medicine, Gainesville, Florida, United States
🇦🇺Royal Brisbane and Women's Hospital, Herston, Queensland, Australia
Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
- Conditions
- Interventions
- First Posted Date
- 2011-08-12
- Last Posted Date
- 2021-07-21
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 173
- Registration Number
- NCT01415427
Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02
- Conditions
- First Posted Date
- 2011-07-06
- Last Posted Date
- 2014-04-02
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 59
- Registration Number
- NCT01387854
- Locations
- 🇺🇸
Children's Hospital and Research Center, Oakland, California, United States
🇩🇪Prof Michael Beck, Mainz, Germany
🇦🇺Women's and Children's hospital, North Adelaide, Australia
Kuvan® in Phenylketonuria Patients Less Than 4 Years Old
- Conditions
- Interventions
- First Posted Date
- 2011-06-20
- Last Posted Date
- 2017-09-15
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 56
- Registration Number
- NCT01376908
- Locations
- 🇬🇧
Research site, London, United Kingdom
🇬🇧Research Site, Birmingham, United Kingdom
A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
- Conditions
- Interventions
- First Posted Date
- 2011-01-12
- Last Posted Date
- 2014-07-07
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 177
- Registration Number
- NCT01275066
A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
- Conditions
- Interventions
- First Posted Date
- 2010-11-16
- Last Posted Date
- 2015-09-30
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 20
- Registration Number
- NCT01242111
Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease
- First Posted Date
- 2010-10-29
- Last Posted Date
- 2018-06-11
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 22
- Registration Number
- NCT01230801
- Locations
- 🇦🇺
Royal Adelaide Hospital, SA Pathology, Adelaide, Adelaide, SA, Australia
🇬🇧Old Queen Elizabeth Hospital, Department of Medicine, Birmingham, United Kingdom
🇬🇧Salford Royal Hospital NHS Trust, Salford, United Kingdom
Safety, Tolerability, and Efficacy Study of rAvPAL-PEG Administered Daily in Subjects With Phenylketonuria (PKU)
- First Posted Date
- 2010-10-01
- Last Posted Date
- 2019-02-26
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 16
- Registration Number
- NCT01212744
- Locations
- 🇺🇸
University of Missouri, Columbia, Missouri, United States
🇺🇸Nationwide Children's Hospital, Columbus, Ohio, United States
🇺🇸The Children's Hospital, Aurora, Colorado, United States
Safety and Therapeutic Effects of Sapropterin Dihydrochloride on Neuropsychiatric Symptoms in Phenylketonuria (PKU) Patients
- Conditions
- Interventions
- First Posted Date
- 2010-05-03
- Last Posted Date
- 2016-02-01
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 206
- Registration Number
- NCT01114737
Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)
- First Posted Date
- 2009-12-23
- Last Posted Date
- 2018-10-16
- Lead Sponsor
- BioMarin Pharmaceutical
- Target Recruit Count
- 18
- Registration Number
- NCT01037309
- Locations
- 🇳🇱
Leiden University Medical Center, Leiden, Netherlands
🇧🇪UZ Leuven, Leuven, Belgium
🇮🇹S.Anna Hospital, Ferrara, Italy