Gene Therapy Restores Hearing in Children with Genetic Deafness
• A clinical trial has demonstrated the successful use of gene therapy to restore hearing in children with DFNB9-related genetic deafness.
• Five out of six children with total deafness recovered their hearing, enabling them to conduct normal conversations after gene therapy.
• The gene therapy introduces a functional OTOF gene via an inactive virus, addressing the root cause of deafness in DFNB9.
• This breakthrough represents a significant milestone, offering a potential treatment for various genetic hearing loss types.
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