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找到 1,838 条关于
“β-Thalassemia”
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1,838
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563
6年前
Gene Therapy Shows Promise in Treating Severe β-Thalassemia
2年前
UK Approves World's First CRISPR Gene Therapy for Sickle Cell Disease and β-Thalassemia
去年
YolTech Therapeutics Launches Clinical Trial for In Vivo Gene Editing Therapy YOLT-204 in Transfusion-Dependent Beta-Thalassemia
11天前
tBE Base Editing Therapy Achieves Durable Remission in Sickle Cell Disease and β-Thalassemia Across Diverse Genetic Backgrounds
去年
Beti-Cel Gene Therapy Shows Sustained Efficacy in Transfusion-Dependent β-Thalassemia
3年前
Mitapivat Shows Durable Improvements in Thalassemia Patients in Phase 2 Extension Study
去年
CorrectSequence Therapeutics Achieves First Successful Sickle Cell Disease Treatment in China Using Base Editing Technology CS-101
3个月前
CorrectSequence's Base-Editing Therapy CS-206 Shows 15-Month VOC-Free Success in Sickle Cell Disease Patient
去年
CRISPR-Based Casgevy Emerges as Preferred Gene Therapy for Beta-Thalassemia, Survey Shows
去年
CDSCO Requests Protocol Revisions for Novartis ITU512 Sickle Cell Disease Trial
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