Safety and Immunogenicity Study of tgAAC09, an HIV Vaccine in an Adeno-associated Virus (AAV) Capsid

计划入组 91 人 · 首次发布于 2009 年 4 月 27 日

Study of RS1 Ocular Gene Transfer for X-linked Retinoschisis

计划入组 12 人 · 首次发布于 2014 年 12 月 17 日

A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)

计划入组 25 人 · 首次发布于 2021 年 3 月 5 日

4D-110

adeno-associated virus (AAV) capsid gene therapy (huntington’s disease)

adeno-associated virus (AAV) capsid gene therapy (rare neurological disease)

4D Molecular Therapeutics

United States

Abeona Therapeutics

United States

Asklepios Biopharmaceutical, Inc.

United States

Novel AAV Capsid Shows Unprecedented Brain Transduction Potential for Gene Therapy

Astellas Licenses AI-Designed AAV Capsid from Dyno Therapeutics for Skeletal Muscle Gene Therapy

Apertura Gene Therapy Launches Open Aperture Program to Democratize Access to CNS-Targeting AAV Capsid