A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations

计划入组 36 人 · 首次发布于 2023 年 3 月 29 日

NG101 AAV Gene Therapy in Subjects With Wet Age-Related Macular Degeneration

计划入组 20 人 · 首次发布于 2023 年 8 月 9 日

AAV Gene Therapy Screening/Observational Protocol (ECLIPSE)

计划入组 37 人 · 首次发布于 2020 年 2 月 17 日

VY-SMN-101

AVTS-001

VY-FXN-01

Abeona Therapeutics

United States

CELL AND GENE THERAPY CATAPULT

United Kingdom

Asklepios Biopharmaceutical, Inc.

United States

VVMF and Mirugen Partner to Advance AAV-Based Gene Therapy Manufacturing for Retinitis Pigmentosa in Australia

Siren Biotechnology Receives FDA Clearance for First AAV-Based Cancer Gene Therapy IND

Ascend Advanced Therapies Achieves GMP Certification for AAV Gene Therapy Quality Control in Munich