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找到 12,570 条关于
“ABCA4 protein”
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去年
SpliceBio Raises $135 Million Series B to Advance Gene Therapy for Stargardt Disease Using Novel Protein Splicing Platform
去年
SpliceBio Initiates First-in-Human Trial of Dual AAV Gene Therapy for Stargardt Disease
8个月前
SpliceBio Advances Gene Therapy for Stargardt Disease with First Patient Dosed in Phase 1/2 Expansion Trial
去年
Gildeuretinol Receives FDA Fast Track and Rare Pediatric Disease Designations for Stargardt Disease
去年
Alkeus' Gildeuretinol Receives FDA Rare Pediatric Disease and Fast Track Designations for Stargardt Disease
去年
Gildeuretinol Receives FDA Fast Track and Rare Pediatric Disease Designations for Stargardt Disease
去年
Gildeuretinol Receives FDA Fast Track and Rare Pediatric Disease Designations for Stargardt Disease
去年
Alkeus Pharmaceuticals' Gildeuretinol Receives FDA Fast Track and Rare Pediatric Disease Designations for Stargardt Disease
去年
Gildeuretinol Receives FDA Fast Track and Rare Pediatric Disease Designations for Stargardt Disease
10个月前
AAVantgarde Secures $141 Million Series B to Advance Gene Therapies for Stargardt Disease and Usher 1B Syndrome
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