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找到 606 条关于
“Adenosine Deaminase”
全部
606
临床试验
295
药物
157
机构
3
资讯
151
2年前
Novel Cytosine Base Editor Restores Dystrophin Expression in DMD Mouse Model
11个月前
AGC Biologics Partners with Rarity PBC to Advance First Commercial Gene Therapy for ADA-SCID "Bubble Baby Disease"
去年
ProQR Therapeutics Receives $8.1M to Advance RNA Editing Therapy for Rett Syndrome
11年前
UCLA Gene Therapy Achieves 100% Cure Rate for Bubble Baby Disease in Clinical Trials
去年
Redwire Secures Contract with Aspera Biomedicines for Space-Based Cancer Research Using ADAR1 Inhibitor Rebecsinib
去年
ProQR Submits First Clinical Trial Application for RNA Editing Platform with AX-0810 Targeting Cholestatic Liver Disease
去年
Novel Therapies Poised to Revolutionize Alpha-1 Antitrypsin Deficiency Treatment
去年
Korro Bio's KRRO-110 Receives Green Light in Australia for AATD Trial
5个月前
ProQR Partners with Ginkgo Bioworks to Accelerate AI-Driven RNA Editing Drug Discovery
11个月前
ProQR Receives EMA Authorization to Begin Phase 1 Trial of AX-0810 RNA Editing Therapy for Cholestatic Diseases
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