Lentiviral (LV) Gene Therapy for Adenosine Deaminase (ADA) Deficiency

计划入组 36 人 · 首次发布于 2011 年 6 月 27 日

Gene Therapy ADA Deficiency

计划入组 8 人 · 首次发布于 2011 年 1 月 19 日

Evaluation of Adenosine Deaminase (ADA) Enzyme Deficiency in Patients With Lymphopenia and/or Elevated Immunoglobulin E

计划入组 100 人 · 首次发布于 2022 年 3 月 29 日

Adenosine deaminase gene therapy(Genetic Therapy, Inc.)

Elapegademase(Oncaspar)

Pegademase

Rna Diagnostics, Inc.

Canada

RNA Pharma, LLC

United States

BioNTech RNA Pharmaceuticals GmbH

Germany

ProQR Therapeutics Receives $8.1M to Advance RNA Editing Therapy for Rett Syndrome

Redwire Secures Contract with Aspera Biomedicines for Space-Based Cancer Research Using ADAR1 Inhibitor Rebecsinib

ProQR Submits First Clinical Trial Application for RNA Editing Platform with AX-0810 Targeting Cholestatic Liver Disease