Natural History of Autosomal Dominant Optic Atrophy (ADOA), Caused by OPA1 Mutation

计划入组 1 人 · 首次发布于 2023 年 11 月 18 日

SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)

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Advanced Characterization of Autosomal Dominant Optic Atrophy

计划入组 50 人 · 首次发布于 2012 年 1 月 31 日

autosomal dominant polycystic kidney disease therapeutics

Autosomal dominant polycystic kidney disease(Maze Therapeutics)

autosomal dominant polycystic kidney disease therapy, Healx

Oculis

Switzerland

Regulus Therapeutics

United States

Orthocell Ltd

PYC Therapeutics Advances Two RNA-Based Therapies for Inherited Blindness Conditions

PYC Therapeutics' RNA Therapies Show Promise in Early-Stage Trials for Genetic Eye Diseases

Stoke Therapeutics Initiates First-in-Human Trial of STK-002 for Rare Genetic Eye Disease ADOA