Natural History Study of Batten Disease

计划入组 10 人 · 首次发布于 2020 年 11 月 25 日

Gene Therapy Trial for CLN6 Batten Disease

计划入组 12 人 · 首次发布于 2026 年 5 月 13 日

Gene Therapy for Children With CLN3 Batten Disease

计划入组 7 人 · 首次发布于 2018 年 12 月 10 日

AT-GTX-502

CLN-619

CLN-049

Beyond Batten Disease Foundation

United States

NHI-1

United States

Xi'an No.1 Hospital

China

Nine-Year-Old Becomes Third Patient Worldwide to Receive Experimental Gene Therapy for Rare Batten Disease

Miglustat Shows Promise in Stabilizing Vision in Juvenile Batten Disease

Batten-1 Advances Toward Pivotal Phase 3 Trial as THX Pharma, Biocodex, and BBDF Unite on International Batten Disease Awareness Day