Treatment of Charcot-Marie-Tooth Disease, Axonal, Type 2S (CMT2S) in an Individual Patient

计划入组 1 人 · 首次发布于 2025 年 11 月 3 日

Ulipristal Acetate In Disease Charcot-Marie-Tooth Type of 1A

计划入组 23 人 · 首次发布于 2015 年 11 月 9 日

Natural History Study for Charcot Marie Tooth Disease

计划入组 10,000 人 · 首次发布于 2023 年 6 月 15 日

Charcot-Marie-Tooth Disease Type 1A(Metagenomi)

Charcot Marie Tooth -Type 2A (MitoRx Therapeutics)

Beclin activator peripheral (Charcot Marie Tooth disease type 1A)

CHAS MARIE

France

MARIE CURIE

United Kingdom

FICHOT MARIE

France

Vanda Pharmaceuticals Initiates First-in-Human Trial of Personalized ASO Therapy VCA-894A for Ultra-Rare CMT2S

Vanda Pharmaceuticals Secures FDA Rare Pediatric Disease Designation for Antisense Oligonucleotide Therapy VCA-894A in CMT2S

Vanda Pharmaceuticals Reports Revenue Increase and Advances Pipeline in Q3 2024