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找到 114,933 条关于
“Charcot-Marie-Tooth disease type 2S”
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去年
Vanda Pharmaceuticals Initiates First-in-Human Trial of Personalized ASO Therapy VCA-894A for Ultra-Rare CMT2S
2个月前
Vanda Pharmaceuticals Secures FDA Rare Pediatric Disease Designation for Antisense Oligonucleotide Therapy VCA-894A in CMT2S
去年
Vanda Pharmaceuticals Reports Revenue Increase and Advances Pipeline in Q3 2024
去年
Advancements in Clinical Outcome Assessments and Biomarkers Pave the Way for CMT Treatment
去年
Augustine Therapeutics Secures €78 Million to Advance HDAC6 Inhibitor for Charcot-Marie-Tooth Disease
11个月前
ReviR Therapeutics Secures FDA Orphan Drug Designation for RTX-117 in Charcot-Marie-Tooth Disease
去年
NMD Pharma's NMD670 Receives FDA Orphan Drug Designation for Charcot-Marie-Tooth Disease
7个月前
NMD Pharma's Ignaseclant Shows Promise in Phase 2a Trial for Charcot-Marie-Tooth Disease
23天前
ReviR Therapeutics Receives FDA Rare Pediatric Disease Designation for RTX-117 in Charcot-Marie-Tooth Disease
2年前
ENCell's Mesenchymal Stem Cell Therapy Shows Promise in First-in-Human Trial for Charcot-Marie-Tooth Disease
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