Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients

计划入组 100 人 · 首次发布于 2024 年 12 月 11 日

Swiss Rare Disease Registry (SRDR)

计划入组 500,000 人 · 首次发布于 2022 年 1 月 5 日

AI-assisted Rare Disease Diagnosis

计划入组 1,056 人 · 首次发布于 2026 年 6 月 16 日

undisclosed rare disease therapeutic (rare disease/eye disease/skin disease)

undisclosed pediatric rare disease therapeutic (rare disease/kidney disease)

undisclosed pediatric rare disease therapeutic (rare disease/immune disease)

CURE RARE DISEASE, INC.

United States

Rare Disease Research, LLC

Rare Disease Therapeutics, Inc.

United States

Cure Rare Disease Secures $7.4 Million CIRM Grant for Novel Gene Therapy Targeting LGMD2i/R9

Cure Rare Disease Advances LGMDR9 Gene Therapy Following Positive FDA Pre-IND Meeting

Form Bio and Cure Rare Disease Partner to Accelerate Gene Therapy Development for Duchenne Muscular Dystrophy