A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants

计划入组 13 人 · 首次发布于 2021 年 5 月 26 日

Transnasal Esophagoscopy (TNE) Esophageal Cancer Screening

计划入组 3 人 · 首次发布于 2022 年 7 月 29 日

A Study to Evaluate the Efficacy and Safety of Factor IX Gene Therapy With PF-06838435 in Adult Males With Moderately Severe to Severe Hemophilia B

计划入组 51 人 · 首次发布于 2019 年 3 月 4 日

Eladocagene exuparvovec(Upstaza)

Fidanacogene elaparvovec(Durveqtix, Beqvez (previously Durveqtix))

Patidistrogene bexoparvovec

FDA Approves Eladocagene Exuparvovec-Tneq (Kebilidi) for AADC Deficiency

FDA Approves Kebilidi Gene Therapy for AADC Deficiency

FDA Approves Kebilidi (eladocagene exuparvovec) Gene Therapy for AADC Deficiency