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找到 84,445 条关于
“Enzyme replacement therapy”
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84,445
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10个月前
FDA Investigates Fatal Adverse Event Linked to Takeda's Adzynma Enzyme Replacement Therapy
9个月前
Health Canada Approves Elfabrio for Fabry Disease Treatment, Expanding Access to PEGylated Enzyme Replacement Therapy
2个月前
Children's Wisconsin Becomes First U.S. Hospital to Administer AVLAYAH, a Blood-Brain Barrier-Crossing Enzyme Replacement Therapy for Hunter Syndrome
去年
China Approves First Domestically Developed Enzyme Replacement Therapy for Gaucher Disease
5年前
Breakthrough Gene Therapy Eliminates Need for Enzyme Replacement in Fabry Disease Patients
去年
Chiesi's ELFABRIO Shows Promise in Phase 3 Trial for Fabry Disease with Twice-Dose Regimen
去年
uniQure's AMT-191 Gene Therapy Shows Sustained Enzyme Activity and ERT Discontinuation in Fabry Disease Phase I/IIa Trial
4个月前
Blackstone Invests $250 Million in Anagram Therapeutics to Advance Novel Enzyme Therapy for Pancreatic Insufficiency
9个月前
BioMarin Awaits Pivotal INZ-701 Trial Results Following $270M Inozyme Acquisition
去年
JCR Pharmaceuticals Completes Enrollment in Global Phase III Trial for Blood-Brain Barrier-Penetrating Hunter Syndrome Therapy
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