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找到 5,906 条关于
“FollowME Fabry Pathfinders”
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5,906
临床试验
5,720
药物
21
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16
资讯
149
去年
Amicus Therapeutics to Present Extensive Research on Fabry and Pompe Diseases at WORLDSymposium 2025
11个月前
EMA Rejects Extended Dosing Regimen for Fabry Disease Treatment Elfabrio
去年
EMA Validates Application for Less Frequent Elfabrio Dosing in Fabry Disease
去年
Less Frequent Elfabrio Dosing Shows Promise in Fabry Disease
去年
FDA Grants Orphan Drug Designation to EXG110 Gene Therapy for Fabry Disease
去年
Sangamo Therapeutics' Fabry Disease Candidate ST-920 Gains Accelerated Approval Pathway
去年
Serum Neurofilament Light Chain Shows Potential as Fabry Disease Biomarker
去年
AceLink's Oral GCS Inhibitor Shows Promising Phase 2 Results in Fabry Disease Treatment
8个月前
Lucerastat Demonstrates Significant Efficacy in Phase 3 Trial for Fabry Disease Treatment
去年
Sangamo's Fabry Disease Gene Therapy ST-920 Poised for Accelerated FDA Approval
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