Natural History of GACI With or Without ARHR2 or PXE

计划入组 80 人 · 首次发布于 2018 年 11 月 29 日

Study of People With Generalized Arterial Calcification of Infancy (GACI) or Autosomal Recessive Hypophosphatemic Rickets Type 2 (ARHR2)

计划入组 48 人 · 首次发布于 2018 年 3 月 27 日

PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency

计划入组 54 人 · 首次发布于 2024 年 3 月 8 日

JACI-35.054

ACI-12589

ACI-7104

Gabi Smartcare

Belgium

Gazi University

Turkey

CACI International

Inozyme's INZ-701 Shows Promise in ENPP1 and ABCC6 Deficiencies

BioMarin's BMN 401 Shows Mixed Results in Phase 3 Trial for Rare ENPP1 Deficiency

Inozyme's INZ-701 Shows Promise in ENPP1 Deficiency Trial with Sustained Phosphate Increases