CD45BE-HSPC + CART-45 Cells

计划入组 42 人 · 首次发布于 2026 年 3 月 5 日

An Open-label Study of a Gene Therapy Product (Vebeglogene Autotemcel) in Transfusion Dependent Beta-Thalassemia

计划入组 6 人 · 首次发布于 2024 年 3 月 13 日

Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector

计划入组 20 人 · 首次发布于 2022 年 6 月 27 日

HBA1 modified CD34+ HSPCs

Autologous CD34+-enriched hematopoietic stem and progenitor cells (Genenta Science)(Temferon)

C46/CCR5/P140K Lentiviral Vector-transduced Autologous HSPCs(NCI)

Cellectis Advances Non-Viral Gene Therapy with Circular DNA Templates and TALE Base Editor Safety Data

UCSF Health Experts Highlight Advances in Hematology at ASH 2024

Scientists Discover Critical Window for In Vivo Gene Therapy in Newborns