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找到 100 条关于
“Hemoglobinopathies”
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100
临床试验
86
药物
3
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1
资讯
10
2个月前
CRISPR Therapeutics and Vertex's Casgevy: First Regulatory-Approved Cell-Based Gene Therapy for Sickle Cell Disease and Beta-Thalassemia
7个月前
Hemex Health Receives FDA Breakthrough Device Designation for Sickle Cell Disease Diagnostic Test
去年
CorrectSequence Therapeutics Achieves First Successful Sickle Cell Disease Treatment in China Using Base Editing Technology CS-101
11天前
tBE Base Editing Therapy Achieves Durable Remission in Sickle Cell Disease and β-Thalassemia Across Diverse Genetic Backgrounds
去年
CDSCO Requests Protocol Revisions for Novartis ITU512 Sickle Cell Disease Trial
上个月
Precision Diabetes and Nagase Diagnostics Announce Exclusive U.S. Commercialization Partnership for Lucica® Glycated Albumin-L, the Only FDA-Cleared Glycated Albumin Assay
3个月前
CorrectSequence's Base-Editing Therapy CS-206 Shows 15-Month VOC-Free Success in Sickle Cell Disease Patient
2年前
Chinese Base Editing Therapy Achieves First Clinical Cure of Beta Thalassaemia
10个月前
California Awards $27 Million to Expand Cell and Gene Therapy Access to Underserved Communities
7天前
Editas Medicine Targets 2026 Patient Dosing for In Vivo CRISPR LDL Therapy EDIT-401