Hereditary Sensory Neuropathy Serine Trial

计划入组 50 人 · 首次发布于 2023 年 11 月 2 日

L-Serine Supplementation in Hereditary Sensory Neuropathy Type 1

计划入组 18 人 · 首次发布于 2012 年 11 月 27 日

Leber Hereditary Optic Neuropathy (LHON) Historical Case Record Survey

计划入组 306 人 · 首次发布于 2013 年 7 月 8 日

AAV2 smCBA based ND4 gene therapy (Leber hereditary optic neuropathy)

RNA actuator therapeutic for hereditary angioedema(CAMP4 Therapeutics)

Diabetic Neuropathy(South Rampart)

Foundation Medicine, Inc.

United States

VCS FOUNDATION LTD

Australia

FLINDERS FOUNDATION

Australia

Wearable Tech Shows Promise in Monitoring CMT Disease Progression for Clinical Trials

EU Approves WAINZUA (Eplontersen) for Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

FDA Approves AstraZeneca and Ionis' Wainua for Hereditary ATTR Polyneuropathy