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找到 47,792 条关于
“Hereditary Spastic Paraplegia Type 4”
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3个月前
Canadian Family Races to Fund Personalized Gene Therapy for Son's Rare Neurodegenerative Disease
去年
FDA Clears BlackfinBio's Gene Therapy Trial for Rare Hereditary Spastic Paraplegia
去年
FDA Clears BlackfinBio's Novel Gene Therapy Trial for Rare Childhood Neurological Disease SPG47
3个月前
CD99L2 Identified as Novel Disease Gene for Spastic Ataxia and Hereditary Spastic Paraplegia
去年
Digital Gait Analysis Shows Promise for Clinical Trials in SPG7
9个月前
Gene Therapy Shows Promise for Hereditary Spastic Paraplegia in Preclinical Study
22天前
Primate-specific Alu-mediated SPAST deletion reveals a druggable zinc–Golgi pathway in dementia-related neurodegeneration
2个月前
Hearing Loss Affects 1 in 4 Adults with Type 2 Diabetes, Systematic Review Reveals
4个月前
Catalent Partners with Elpida Therapeutics to Advance AAV Gene Therapy for Ultra-Rare SPG50 Disease
3个月前
LifeArc Partners with Elpida Therapeutics to Advance Gene Therapies for Ultra-Rare Pediatric Neurodegenerative Diseases
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