Palliative Care Needs of Children With Rare Diseases and Their Families

计划入组 480 人 · 首次发布于 2025 年 4 月 22 日

National Eye Institute Biorepository for Retinal Diseases

计划入组 650 人 · 首次发布于 2011 年 12 月 21 日

Heart Institute BioRepository (HIBR) for Pediatric Heart Disease

计划入组 5,000 人 · 首次发布于 2026 年 3 月 17 日

undisclosed pediatric rare disease program (rare CNS diseases)

RARE DISEASES(Gero)

undisclosed pediatric rare disease therapeutic (rare disease/kidney disease)

RECORDATI RARE DISEASES

France

Recordati Rare Diseases, Inc.

United States

HRA Pharma Rare Diseases SAS

France

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