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找到 46,298 条关于
“LAMA2 related muscular dystrophy”
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46,298
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8个月前
Modalis Publishes Breakthrough CRISPR Gene Activation Study for Rare Muscular Dystrophy Treatment
11个月前
DINAMIQS Opens Switzerland's First cGMP Viral Vector Manufacturing Facility, Partners with SEAL Therapeutics for Muscular Dystrophy Gene Therapy
去年
Modalis Therapeutics Receives FDA Orphan Drug Designation for MDL-101 in LAMA2-CMD Treatment
去年
FDA Grants Orphan Drug Designation to Modalis Therapeutics' MDL-101 for LAMA2-CMD
去年
FDA Grants Orphan Drug Designation to MDL-101 for Congenital Muscular Dystrophy Type 1A
上个月
Sarcomatrix Advances S-969 Toward First-in-Human Dosing With SarcoVista Modeling and Expanded CMC Package
去年
MDL-101 Receives FDA Rare Pediatric Disease Designation for LAMA2-CMD Treatment
2年前
Capricor Therapeutics Gains FDA Alignment on HOPE-3 Trial Design for CAP-1002 in Duchenne Muscular Dystrophy
2年前
Genethon's AAV Gene Therapy GNT0004 Shows Promise in Duchenne Muscular Dystrophy Trial
3年前
FDA Approves Elevidys, a Gene Therapy for Duchenne Muscular Dystrophy
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