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找到 1,354 条关于
“LCA-AIPL1”
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1,354
临床试验
965
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225
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106
资讯
58
去年
Breakthrough Gene Therapy Restores Vision in Children with Rare Genetic Blindness
去年
MeiraGTx Advances Gene Therapy Pipeline with FDA RMAT Designation and Pivotal Trial Progress
去年
MeiraGTX's Gene Therapy Shows Promising Visual Benefits in Children with Rare Genetic Blindness
2年前
CRISPR Gene Editing Shows Promise in Treating Rare Form of Blindness
去年
Opus Genetics Advances LCA5 Gene Therapy Program with First Pediatric Patient Dosing and Promising Adult Data
去年
Ocugen's OCU400 Gene Therapy Shows Promise in Retinitis Pigmentosa Phase 1/2 Trial
去年
Children's Hospital Los Angeles Celebrates Milestone with 100th Retinal Gene Therapy Procedure
去年
Opus Genetics to Present 6-Month Data on OPGx-LCA5 Gene Therapy for LCA5-Associated Inherited Retinal Disease
去年
Atsena Therapeutics and Nippon Shinyaku Partner to Advance Gene Therapy for LCA1
5个月前
Six-Year-Old Girl Regains Vision Through Groundbreaking NHS Gene Therapy for Leber's Congenital Amaurosis
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