Intravenous ACP-501 for Familial LCAT Deficiency (rhLCAT)

计划入组 1 人 · 首次发布于 2021 年 2 月 4 日

LCAT (Lecithin Cholesterol Acyl Transferase) Natural History Study

计划入组 40 人 · 首次发布于 2024 年 1 月 22 日

Mendelian Reverse Cholesterol Transport Study

计划入组 30 人 · 首次发布于 2013 年 2 月 1 日

LCAT-GMAC

genetically modified adipose cell therapy

CDKL5 deficiency disorder therapeutic program (Vyant Bio Inc/Cyclica Inc)

Rockwell Medical

United States

Ai-Media Technologies Ltd

United States

Bio-Cat, Inc.

United States

EMA Provides Positive Feedback on ABIONYX Pharma's CER-001 for LCAT Deficiency

ABIONYX Secures Up to €33M and Launches Pivotal Phase 2b Trial of CER-001 in Sepsis

FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency