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找到 3,067 条关于
“Leber's congenital amaurosis”
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3,067
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4个月前
Six-Year-Old Girl Regains Vision Through Groundbreaking NHS Gene Therapy for Leber's Congenital Amaurosis
6年前
Free Genetic Testing Initiative Accelerates Drug Development for Inherited Retinal Diseases
去年
Variant Secures EMA Endorsement for VAR002 Gene Therapy Targeting Inherited Retinal Dystrophies
6年前
First In Vivo CRISPR Therapy Dosed in Clinical Trial for Congenital Blindness
去年
HuidaGene's CRISPR/Cas13 RNA-Editing Therapy HG202 Cleared for US Trial in Macular Degeneration
去年
FDA Approves Neurocrine's Crenessity (crinecerfont) for Congenital Adrenal Hyperplasia
去年
Ocugen to Highlight Retinal Gene Therapy Progress at Clinical Showcase
去年
Sidra Medicine Conducts First Clinical Trial for Pediatric Congenital Hyperinsulinism
9个月前
FDA Approves Grifols' Fesilty for Congenital Fibrinogen Deficiency Treatment
去年
Innovative Prenatal Therapy Saves Children with Congenital Vascular Malformations in Poland
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