Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)

计划入组 9 人 · 首次发布于 2024 年 2 月 28 日

A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I

计划入组 9 人 · 首次发布于 2019 年 1 月 23 日

A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I

首次发布于 2019 年 1 月 31 日

focal adhesion kinase

Leukocyte interleukin

Dialyzable leukocyte extract

Universitetet i Oslo

Norway

I-SHOU UNIVERSITY

Taiwan

i-SENS, Inc.

South Korea

Rocket Pharmaceuticals Advances Gene Therapy Pipeline for Rare Disorders

Gene Therapy Shows Promising Results in Children with Rare Immune Disorder LAD-I

EMA Initiates Review of Rocket Pharma's Gene Therapy for Fanconi Anaemia