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找到 1,225 条关于
“Lyso-Gb1”
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1,225
临床试验
773
药物
378
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3
资讯
71
去年
Spur Therapeutics' FLT201 Gene Therapy Shows Promise in Gaucher Disease with FDA Alignment on Phase 3
8个月前
Spur Therapeutics to Present Two-Year Clinical Data for FLT201 Gene Therapy in Gaucher Disease at WORLDSymposium
去年
Precision Genomic Profiling Reveals Multiple Molecular Diagnoses in Gaucher Disease Patients with Atypical Presentations
去年
Elfabrio Shows Promise in Phase 3 BRIGHT Study for Fabry Disease
去年
uniQure's AMT-191 Gene Therapy Shows Sustained Enzyme Activity and ERT Discontinuation in Fabry Disease Phase I/IIa Trial
去年
Sangamo's Gene Therapy Shows Sustained Benefits in Fabry Disease Patients with Improved Kidney Function
去年
Less Frequent Elfabrio Dosing Shows Promise in Fabry Disease
去年
AceLink Therapeutics' AL01211 Shows Promising Safety and Biomarker Reduction in Phase 2 Fabry Disease Trial
10个月前
Sangamo Therapeutics Advances Fabry Disease Gene Therapy Toward FDA Submission Following Positive Clinical Data
2年前
Lisocabtagene Maraleucel Shows Consistent Benefit in High-Risk CLL Subgroups
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