Safety and Efficacy of Encapsulated Allogeneic MPS-1 Therapy

首次发布于 2022 年 12 月 27 日

MPS (RaDiCo Cohort) (RaDiCo-MPS)

计划入组 1,000 人 · 首次发布于 2023 年 9 月 14 日

Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI

计划入组 6 人 · 首次发布于 2023 年 5 月 6 日

CPS2

MPSP-001

MSP2-C1

New At-Home Urine Test Accurately Detects Aggressive Prostate Cancer, Reducing Need for Invasive Procedures

REGENXBIO and Nippon Shinyaku Partner to Advance Gene Therapies for MPS I and MPS II

Denali Therapeutics Plans Accelerated Approval Filing for Tividenofusp Alfa in MPS II