Oral or Intra Muscular Vitamin D2 Vs Oral or Intra Muscular Vitamin D3 in Treatment of Vitamin D Deficiency

计划入组 100 人 · 首次发布于 2024 年 9 月 30 日

Energy Deficiency on Hormones in Contraceptive Users

计划入组 30 人 · 首次发布于 2026 年 6 月 16 日

Understanding the Spectrum of ENPP1 Deficiency and Acute ABCC6 Deficiency

计划入组 38 人 · 首次发布于 2020 年 5 月 4 日

CDKL5 deficiency disorder therapeutic program (Vyant Bio Inc/Cyclica Inc)

WWOX gene therapy(Mahzi Therapeutics/ Hebrew University)

CBS-deficiency(Mitorx Therapeutics)

Rockwell Medical

United States

Ai-Media Technologies Ltd

United States

Krajská zdravotní, a.s. - Masarykova nemocnice v Ústí nad Labem, o.z.

Czech Republic

High-dose vitamin B3 offers new hope for children with rare NAXD deficiency

FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency

FDA Approves Kebilidi, First Gene Therapy for AADC Deficiency