National Registry of Rare Kidney Diseases

计划入组 35,000 人 · 首次发布于 2023 年 10 月 4 日

French National Database of Rare Dermatological Cancers

计划入组 9,000 人 · 首次发布于 2017 年 7 月 7 日

Clean Air for Rare MUcociliary Clearance dIsorders

计划入组 62 人 · 首次发布于 2026 年 2 月 18 日

LUNAR-RARE2

trimethylangelicin (Rare Partners)

polyoma virus specific T cells

Institute For Neurodegenerative Disorders

United States

LYSOSOMAL AND RARE DISORDERS RESEARCH AND TREATMENT CENTER, INC.

United States

NATIONAL INSTITUTE OF NEUROLOGICAL DISORDERS AND STROKE

United States

FDA Expands Rare Disease Research Support with $27 Million in Grants and New Innovation Hub

Soticlestat Fails to Meet Primary Endpoints in Phase III Trials for Dravet and Lennox-Gastaut Syndromes

CDSCO Approves Novartis' Protocol Amendment for Iptacopan Study in Rare Kidney Disorders