Niemann-Pick Type C Disease(Alectos)

oligonucleotide therapy (Niemann-Pick type C disease)

glucocerebrosidase II inhibitors (Niemann-Pick type C disease)

AAV gene therapy (Niemann Pick type C disease) (Amicus/ University of Pennsylvania)

Niemann Pick Type C(Scenic Biotech)

Niemann-Pick Type A disease therapeutics

Niemann-Pick type A disease gene therapy (Sanofi)

TX-01

Recombinant Ebola Virus Disease Vaccine(Adenovirus Type 5 Vector)

Rx

C-53