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找到 124,717 条关于
“Niemann-Pick type C disease”
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124,717
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去年
EMA Recommends Approval of Aqneursa for Niemann-Pick Type C Disease Treatment
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
去年
FDA Approves Miplyffa for Niemann-Pick Type C Disease, Offering New Hope for Rare Genetic Disorder
3个月前
THX Pharma and Exeltis Secure EMA Paediatric Committee Approval for TX01, Unlocking PUMA Pathway for Niemann-Pick Type C Disease
7个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
2年前
FDA Advisory Committee Supports Arimoclomol for Niemann-Pick Disease Type C
9个月前
FDA Grants Breakthrough Therapy Designation to Adrabetadex for Infantile-Onset Niemann-Pick Disease Type C
去年
FDA Approves Zevra Therapeutics' Miplyffa for Niemann-Pick Disease Type C, Stock Surges
去年
FDA Approves Arimoclomol for Niemann-Pick Disease Type C After Multiple Failed Trials
3年前
IntraBio Completes Over-Enrollment for Pivotal Niemann-Pick Disease Type C Trial, Data Expected Q2 2023
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