A Study to Evaluate DCR-PHXC in Children and Adults With Primary Hyperoxaluria Type 1 and Primary Hyperoxaluria Type 2

计划入组 35 人 · 首次发布于 2019 年 2 月 20 日

Evaluation of the Efficacy and Safety of Stiripentol in Patients 6 Years and Older With Primary Hyperoxaluria Type 1, 2 or 3

计划入组 42 人 · 首次发布于 2024 年 6 月 18 日

Nedosiran in Pediatric Patients From Birth to 11 Years of Age With PH and Relatively Intact Renal Function

计划入组 27 人 · 首次发布于 2021 年 8 月 11 日

Primary hyperoxaluria type 1(Metagenomi)

Primary Hyperoxaluria T.1(CorrGene Biotechnology)

Poliovirus type 2 antigen (formaldehyde inactivated)(Ipol, Kinrix, Pediarix, Pentacel, Quadracel, Vaxelis)

PRIMARY PHARMACEUTICALS, INC.

United States

PRIMARY HEALTH CARE CORPORATION

Qatar

MEREO BIOPHARMA 2 LIMITED

United Kingdom

Oral Drug N-PPG Shows Complete Prevention of Kidney Stones and Death in Rare Disease Model

ABO-101 Gene Editing Therapy for Primary Hyperoxaluria Type 1 Granted Orphan Drug Designation by European Commission

Arbor Biotechnologies' ABO-101 Receives FDA Clearance for Phase 1/2 Trial in Primary Hyperoxaluria Type 1