Pyruvate Kinase Deficiency Global Longitudinal Registry

计划入组 500 人 · 首次发布于 2018 年 3 月 29 日

Pyruvate Kinase Deficiency Natural History Study

计划入组 254 人 · 首次发布于 2014 年 2 月 3 日

Pyruvate Kinase Deficiency Epidemiological Study (PIECE)

计划入组 75 人 · 首次发布于 2019 年 3 月 7 日

Mitapivat(Pyrukynd 5 Mg 4-week, Pyrukynd)

C₂₄H₂₆N₄O₃S

pyruvate kinase M2 activators

Pyruvate

Rockwell Medical

United States

Exelixis, Inc.

United States

Inhibikase Therapeutics

United States

Agios Submits New Drug Application to FDA for Mitapivat for Treatment of Adults with Pyruvate Kinase Deficiency

FDA Approves Pyrukynd as First Treatment for Pyruvate Kinase Deficiency

FDA Approves Pyrukynd (mitapivat) for Hemolytic Anemia in Adults with Pyruvate Kinase Deficiency