RPE65 retinal dystrophy | Clinical Trials Search

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14,521 results for “RPE65 retinal dystrophy”

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Gene Therapy in Subjects With Biallelic RPE65 Mutation-associated Retinal Dystrophy

9 participants · First posted May 15, 2023

Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy

4 participants · First posted Aug 18, 2020

Active, not recruiting

Efficacy and Safety of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

30 participants · First posted Jul 8, 2025

Active, not recruiting

Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

9 participants · First posted Jan 9, 2024

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

87 participants · First posted Jul 24, 2018

Active, not recruiting

Fellow-eye Study (FE) of LX101 in Subjects With Inherited Retinal Dystrophy

9 participants · First posted Jan 18, 2024

Clinical Gene Therapy Protocol for the Treatment of Retinal Dystrophy Caused by Defects in RPE65

9 participants · First posted Dec 21, 2011

Long-Term Follow-Up Gene Therapy Study for Leber Congenital Amaurosis OPTIRPE65 (Retinal Dystrophy Associated With Defects in RPE65)

15 participants · First posted Oct 27, 2016

Active, not recruiting

Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

41 participants · First posted Jul 27, 2018

Natural History of Patients With Inherited Retinal Diseases Due to Mutations in RPE65 Gene

60 participants · First posted Aug 25, 2020

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