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找到 124,527 条关于
“Rare Pediatric Disease Designation”
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124,527
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2年前
Longboard Pharmaceuticals Launches Phase 3 Trial of Bexicaserin for Dravet Syndrome
去年
Zaltenibart Receives FDA Rare Pediatric Disease Designation for C3 Glomerulopathy
去年
Elraglusib Receives FDA Rare Pediatric Disease Designation for Ewing Sarcoma
3个月前
RedHill's Opaganib Receives FDA Rare Pediatric Disease Designation for Neuroblastoma
2年前
FDA Grants Rare Pediatric Disease Designation to Cartesian's Descartes-08 for Juvenile Dermatomyositis
去年
FDA Discontinues Rare Pediatric Disease Designation Program Despite Rising Approval Trends
去年
EyeDNA's HORA-PDE6b Receives FDA Rare Pediatric Disease Designation for PDE6b Retinitis Pigmentosa
去年
Elixirgen Therapeutics Receives FDA Rare Pediatric Disease Designation for EXG-34217 in Dyskeratosis Congenita
去年
FDA Ends Rare Pediatric Disease Designation Program After Decade of Mixed Results
去年
FDA Grants Rare Pediatric Disease Designation to Modalis Therapeutics' MDL-101 for Genetic Disorder Treatment
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