Functional Genomics of Rare Genetic Diseases: Realization of Innovative Tools With High Diagnostic Power

计划入组 300 人 · 首次发布于 2019 年 11 月 5 日

Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients

计划入组 100 人 · 首次发布于 2024 年 12 月 11 日

Rare CFTR Mutation Cell Collection Protocol (RARE)

计划入组 500 人 · 首次发布于 2017 年 5 月 22 日

LUNAR-RARE2

trimethylangelicin (Rare Partners)

Live Bifidobacterium Power（Livzon Pharma）

Forgent Power Solutions

Spain

Power to Decide

United States

Power Life Sciences, Inc.

United States

FDA Grants Orphan Drug Designation to CUHK's Novel Peptide Drug Candidate

Global Genes Partners with Citizen Health to Power RARE-X Rare Disease Data Platform

Promising Pathway Act 2.0 Aims to Expedite Rare Disease Drug Approvals