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找到 10,808 条关于
“SGSH gene”
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10,808
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去年
Ultragenyx's UX111 Gene Therapy Shows Promise in Sanfilippo Syndrome Type A
4个月前
Orchard Therapeutics Receives Innovation Passport for Gene Therapy OTL-201 Targeting Rare Sanfilippo Syndrome
去年
FDA Issues Complete Response Letter for Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A
去年
Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A Receives FDA Priority Review
昨天
FDA Approves Fayuvi, First-Ever Gene Therapy for Sanfilippo Syndrome Type A
4年前
Ultragenyx Acquires Global Rights to Abeona's Gene Therapy for Sanfilippo Syndrome Type A
3年前
Ultragenyx's UX111 Gene Therapy Shows Sustained Efficacy in MPS IIIA Patients
上个月
Dongguk University Researchers Develop Electromagnetically Controllable Gene Switch for Remote Gene Therapy
去年
StitchR Gene Therapy Enables Treatment for Muscular Dystrophies and Large-Gene Diseases
去年
Gene Therapy and Gene Editing Show Promise in HIV Treatment
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