Registry and Natural History Study for Early Onset Hereditary Spastic Paraplegia

计划入组 700 人 · 首次发布于 2021 年 1 月 15 日

Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)

计划入组 5 人 · 首次发布于 2025 年 4 月 28 日

Consequences of Mutations in the SPG7 Gene at the Heterozygous State

计划入组 11 人 · 首次发布于 2021 年 11 月 19 日

FDA Clears BlackfinBio's Novel Gene Therapy Trial for Rare Childhood Neurological Disease SPG47

FDA Clears BlackfinBio's Gene Therapy Trial for Rare Hereditary Spastic Paraplegia

Digital Gait Analysis Shows Promise for Clinical Trials in SPG7