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找到 327,146 条关于
“Sanfilippo A”
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327,146
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去年
Ultragenyx's UX111 Gene Therapy Shows Promise in Sanfilippo Syndrome Type A
17小时前
FDA Approves Fayuvi, First-Ever Gene Therapy for Sanfilippo Syndrome Type A
去年
Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A Receives FDA Priority Review
去年
FDA Issues Complete Response Letter for Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A
11个月前
Spruce Biosciences Secures $50M to Advance Sanfilippo Syndrome Type B Therapy Toward BLA Submission
4年前
Ultragenyx Acquires Global Rights to Abeona's Gene Therapy for Sanfilippo Syndrome Type A
去年
Ultragenyx Initiates Phase 3 Aspire Study of GTX-102 for Angelman Syndrome
去年
FDA Delays Gene Therapy Approval for Sanfilippo Syndrome Until 2026, Affecting Young Patients
去年
GC Biopharma and Novel Pharma Initiate Phase I Trial of GC1130A for Sanfilippo Syndrome Type A
2年前
JCR Pharmaceuticals' JR-441 Receives Clearance for Phase I MPS IIIA Trial in Japan
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