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找到 7,978 条关于
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去年
UMass Chan Gene Therapy Shows Biochemical Correction in GM2 Gangliosidosis Phase I/II Trial
去年
MEDIPAL Holdings and JCR Pharmaceuticals Partner on Novel GM2 Gangliosidosis Therapy JR-479
7个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
去年
Azafaros to Present at J.P. Morgan's 43rd Annual Healthcare Conference
10个月前
Polaryx Therapeutics Secures Nasdaq Listing Ahead of Phase 2 Trial for Rare Lysosomal Storage Disorders
上个月
Andelyn Biosciences Partners with Queen's University to Manufacture AAV9-GM2 Gene Therapy for GM2 Gangliosidoses
6年前
Sanofi Pivots R&D Strategy, Discontinues Diabetes Research to Focus on Novel Therapeutics
去年
Myrtelle's rAAV-Olig001-ASPA Gene Therapy Shows Promise in Canavan Disease Trial
2年前
BridgeBio's BBP-812 Receives FDA RMAT Designation for Canavan Disease Gene Therapy
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